Rare Disease: An Integrated, Patient-centered Approach to Research and Commercialization

September 29, 2016

Although rare diseases individually affect very few patients, the collective impact is staggering. Globally, the list of rare diseases has grown to approximately 7,000, and 350 million people are living with a rare disease. These diseases are serious, often life-threatening, and approximately half of those affected are children. The lack of available treatments leaves patients and their families searching for new options and new hope. Regulatory incentives such as the orphan products designation and the availability of Pediatric Rare Disease Priority Review Vouchers have increased the interest in rare disease research.

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All Valley Home Health Care & Nursing

All Valley Home Health Care and Nursing was founded in 2005 by Brent Owens, Barbara Owens, and Becky Camara. Brent Owens started as a caregiver, serving as a companion for an elderly patient in the hospital, and quickly moved up to become a client care coordinator, and eventually, purchasing the company with help from his mother, Barbara and sister, Becky...

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All Valley Home Health Care & Nursing

All Valley Home Health Care and Nursing was founded in 2005 by Brent Owens, Barbara Owens, and Becky Camara. Brent Owens started as a caregiver, serving as a companion for an elderly patient in the hospital, and quickly moved up to become a client care coordinator, and eventually, purchasing the company with help from his mother, Barbara and sister, Becky...

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